Exagamglogene autotemcel (exa-cel) is a nonviral cell therapy designed to reactivate fetal hemoglobin synthesis by means of ex vivo clustered regularly interspaced short palindromic repeats ...
Sickle cell disease (SCD) is a group of genetic blood disorders. A person inherits SCD from their parents when they inherit two copies of the sickle cell gene, one from each parent. This hereditary ...
Andrew Campbell, MD, is a distinguished leader in the field of sickle cell disease research and treatment. Currently serving as the director of the Comprehensive Sickle Cell Disease (SCD) Program at ...