Life with Duchenne MD rarely follows a neat arc, writes columnist. That forces people to revisit the script and constantly ...

A mother's love drives her to pursue experimental treatment as two of her four children battle a rare genetic disease that ...

Defeat Duchenne Canada (DDC) is proud to mark 30 years of funding research into Duchenne muscular dystrophy by announcing a major milestone: the organization has now surpassed $20 million invested in ...

By Mariam Sunny Jan 26 (Reuters) - Sarepta Therapeutics' gene therapy for Duchenne muscular dystrophy slowed disease ...

Sarepta reports positive, statistically significant results in a study evaluating the efficacy of its blockbuster gene ...

On a Monday conference call, Sarepta CEO Doug Ingram said new long-term data should help “rebalance the discussion” ...

While it’s established that Duchenne muscular dystrophy (DMD) causes a loss of muscle mass and strength, few studies have examined the gastrointestinal issues tied to DMD. Initial fractures are the ...

When you're diagnosing a child with Duchenne muscular dystrophy, says Alexandra Bonner, MD, of Cleveland Clinic, it's important to not only determine if she's a carrier of the gene mutation that ...

Quadriplegic and bedridden in a prefabricated home, 36-year-old Li Xia can only move one finger and one toe -- yet he runs a ...

Jan 26 (Reuters) - Sarepta Therapeutics' gene therapy for a progressive muscle‑wasting disorder showed sustained benefit in ...